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Updates from our team at the Annual AP-4-HSP Research Conference

Posted on February 1, 2026 by Darius Ebrahimi-Fakhari
Posted in 2025

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Dr. Kathryn Yang gives a seminar at BC Children’s Hospital in Vancouver, Canada.
Updates on the Phase 1/2 Clinical Trial: Safety and Efficacy of AAV9/​AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47) [NCT06948019] at 1st Boston Children’s Hospital Gene Therapy Retreat
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