Updates on the Phase 1/2 Clinical Trial: Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47) [NCT06948019] at 1st Boston Children’s Hospital Gene Therapy Retreat Posted on February 1, 2026 by Darius Ebrahimi-Fakhari