Thakur G, Dhanukate R, Mou Y, Kunhiraman P, Khadilkar A, Srivastava S, Alecu JE, Ebrahimi-Fakhari D, Chen Z, Blackstone C, Li XJ. LXR agonist rescues synaptic dysfunction and degeneration in SPG3A patient-specific iPSC-derived neurons. Acta Neuropathol Commun. 2025 Nov 17;13(1):236. doi: 10.1186/s40478-025-02134-5. PMID: 41250225; PMCID: PMC12625089.

